DPRs as key drivers of C9ORF72 ALS/FTD (opens in new tab)
Blocking DPRs improved behavioral, cellular, and molecular outcomes in mouse models and patient iPSC-derived neurons, demonstrating DPRs as key driver
Read the original articleBlocking DPRs improved behavioral, cellular, and molecular outcomes in mouse models and patient iPSC-derived neurons, demonstrating DPRs as key driver
Read the original article